Diseases and medical issues by Fabricio Carlos Sena

Alzheimer

2025-05-20 21:45:50 UTC

Gene therapy holds promise for Alzheimer's treatment, not as a cure, but as a potential way to slow progression, reduce symptoms, and delay the onset of the disease. It works by modifying or replacing faulty genes, targeting pathways like Aβ and tau, and enhancing neuroprotection. While promising, significant challenges remain before widespread clinical application, including managing risks associated with delivery methods and addressing high costs.

Cancer

2025-05-20 21:46:33 UTC

gene therapy is one of the most progressive cancer treatments currently being studied in clinical trials.

Recent clinical trials of second and third generation vaccines have shown encouraging results with a wide range of cancers, including lung cancer, pancreatic cancer, prostate cancer and malignant melanoma.

Oncolytic virotherapy, which uses viral particles that replicate within the cancer cell to cause cell death, is an emerging treatment modality that shows great promise, particularly with metastatic cancers.

Site: NIH

Muscular dystrophy

2025-05-20 21:47:40 UTC

While gene therapy doesn't offer a cure for Duchenne muscular dystrophy and can't bring back muscle cells already lost, it shows promise in stabilizing the progression of symptoms and, in some individuals, improving strength and endurance at an age when children with Duchenne usually become weaker.